We've found
734 Metabolic
clinical trials
We've found
734 Metabolic
clinical trials
Gastroenterology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Cardiology / Vascular Diseases, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
Study of ISIS 678354 (AKCEA-APOCIII-LRx) in Patients With Hypertriglyceridemia and Established Cardiovascular Disease (CVD)
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Gaucher's Disease Clinical Trial
Updated: 6/23/2005
Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease
Status: Enrolling,
Phase
II
Updated: 6/23/2005
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Hematology, Neurology, Pharmacology / Toxicology, Rheumatology, Orthopedics / Podiatry, Other, Reproductive Clinical Trial
Updated: 6/22/2011
Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
Status: Enrolling,
Phase
I, II
Updated: 6/22/2011
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 6/25/2013
Pulmonary Disease and Exercise Tolerance in Boys With Fabry Disease
Status: Enrolling
Updated: 6/25/2013
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Cardiology / Vascular Diseases, Neurology, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Cardiology / Vascular Diseases, Endocrinology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
Effects of DPP-4 Inhibition on Triglycerides
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Hematology, Pharmacology / Toxicology, Other Clinical Trial
Updated: 8/10/2015
Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children
Status: Enrolling
Updated: 8/10/2015
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Endocrinology, Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
Longitudinal Studies of Brain Structure and Function in MPS Disorders
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Neurology, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/1/2015
Pharmacokinetics and Clinical Response of Tolvaptan in Neurocritical Care Patients
Status: Enrolling
Updated: 12/1/2015
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology, Psychiatry / Psychology Clinical Trial
Updated: 12/31/1969
Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I
Status: Enrolling
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Physician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry Disease
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Cardiology / Vascular Diseases, Endocrinology, Neurology, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Fatty Acid Oxidation Defects and Insulin Sensitivity
Status: Enrolling
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
MPS I Clinical Trial
Updated: 12/31/1969
Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-318 in Subjects With MPS I
Status: Enrolling,
Phase
I
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Ornithine Transcarbamylase (OTC) Deficiency Clinical Trial
Updated: 12/31/1969
Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset OTC Deficiency
Status: Enrolling,
Phase
I, II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Ornithine Transcarbamylase (OTC) Deficiency Clinical Trial
Updated: 12/31/1969
Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset OTC Deficiency
Status: Enrolling,
Phase
I, II
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Gaucher Disease Clinical Trial
Updated: 12/31/1969
Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Gaucher Disease Clinical Trial
Updated: 12/31/1969
Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged 12 to
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged 12 to
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Efficacy and Safety of Lucerastat Oral Monotherapy in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Cardiology / Vascular Diseases, Endocrinology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
Habitual Diet and Avocado Trial
Status: Enrolling
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Extension Study of 1 mg/kg Pegunigalsidase Alfa in Patients With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Extension Study of 1 mg/kg Pegunigalsidase Alfa in Patients With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Open Label Extension of 2 mg/kg Pegunigalsidase Alfa (PRX-102) Every 4 Weeks in Adult Fabry Disease Patients
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Open Label Extension of 2 mg/kg Pegunigalsidase Alfa (PRX-102) Every 4 Weeks in Adult Fabry Disease Patients
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Gastroenterology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Gastroenterology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Gaucher Disease Clinical Trial
Updated: 12/31/1969
A Long-term Follow-up Study of Gaucher Disease
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Cardiology / Vascular Diseases, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
Study of ISIS 678354 (AKCEA-APOCIII-LRx) in Patients With Hypertriglyceridemia and Established Cardiovascular Disease (CVD)
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Neurology, Pharmacology / Toxicology, Psychiatry / Psychology, Reproductive Clinical Trial
Updated: 2/3/2016
Screening for Metabolic Problems in Mothers of Children With Autism and Typically Developing Children
Status: Upcoming
Updated: 2/3/2016
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Evaluation of Phenotypic Variability in Fabry Disease
Status: Upcoming,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Fabry Disease Clinical Trial
Updated: 12/31/1969
Pre-Clinical White Matter Changes and Associated Connectivity Effects in Fabry Disease
Status: Upcoming
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Pharmacology / Toxicology Clinical Trial
Updated: 5/15/2017
Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and II
Status: Upcoming,
Phase
I, II
Updated: 5/15/2017
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)
Click here to add this to my saved trials
![](https://www.clinicaltrialsgps.com/wp-content/themes/GPS/media//img/tooltip-arrow.png)