We've found
734 Metabolic
clinical trials
Gastroenterology, Pharmacology / Toxicology Clinical Trial
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Cardiology / Vascular Diseases, Pharmacology / Toxicology Clinical Trial
Study of ISIS 678354 (AKCEA-APOCIII-LRx) in Patients With Hypertriglyceridemia and Established Cardiovascular Disease (CVD)
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Gaucher's Disease Clinical Trial
Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease
Status: Enrolling,
Phase
II
Updated: 6/23/2005
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Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Hematology, Neurology, Pharmacology / Toxicology, Rheumatology, Orthopedics / Podiatry, Other, Reproductive Clinical Trial
Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
Status: Enrolling,
Phase
I, II
Updated: 6/22/2011
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Fabry Disease Clinical Trial
Pulmonary Disease and Exercise Tolerance in Boys With Fabry Disease
Status: Enrolling
Updated: 6/25/2013
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Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Cardiology / Vascular Diseases, Neurology, Pharmacology / Toxicology, Other Clinical Trial
Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism
Status: Enrolling,
Phase
Updated: 12/31/1969
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Cardiology / Vascular Diseases, Endocrinology, Pharmacology / Toxicology Clinical Trial
Effects of DPP-4 Inhibition on Triglycerides
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
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Pharmacology / Toxicology, Other Clinical Trial
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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Pharmacology / Toxicology, Other Clinical Trial
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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Endocrinology, Hematology, Pharmacology / Toxicology, Other Clinical Trial
Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children
Status: Enrolling
Updated: 8/10/2015
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Endocrinology, Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Longitudinal Studies of Brain Structure and Function in MPS Disorders
Status: Enrolling,
Phase
Updated: 12/31/1969
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Neurology, Pharmacology / Toxicology, Other Clinical Trial
Pharmacokinetics and Clinical Response of Tolvaptan in Neurocritical Care Patients
Status: Enrolling
Updated: 12/1/2015
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Pharmacology / Toxicology, Psychiatry / Psychology Clinical Trial
Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I
Status: Enrolling
Updated: 12/31/1969
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Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Physician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry Disease
Status: Enrolling,
Phase
Updated: 12/31/1969
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Cardiology / Vascular Diseases, Endocrinology, Neurology, Pharmacology / Toxicology, Other Clinical Trial
Fatty Acid Oxidation Defects and Insulin Sensitivity
Status: Enrolling
Updated: 12/31/1969
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MPS I Clinical Trial
Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-318 in Subjects With MPS I
Status: Enrolling,
Phase
I
Updated: 12/31/1969
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Ornithine Transcarbamylase (OTC) Deficiency Clinical Trial
Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset OTC Deficiency
Status: Enrolling,
Phase
I, II
Updated: 12/31/1969
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Ornithine Transcarbamylase (OTC) Deficiency Clinical Trial
Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset OTC Deficiency
Status: Enrolling,
Phase
I, II
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Gaucher Disease Clinical Trial
Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
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Gaucher Disease Clinical Trial
Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged 12 to
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged 12 to
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Efficacy and Safety of Lucerastat Oral Monotherapy in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Cardiology / Vascular Diseases, Endocrinology, Pharmacology / Toxicology Clinical Trial
Habitual Diet and Avocado Trial
Status: Enrolling
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Extension Study of 1 mg/kg Pegunigalsidase Alfa in Patients With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Extension Study of 1 mg/kg Pegunigalsidase Alfa in Patients With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Open Label Extension of 2 mg/kg Pegunigalsidase Alfa (PRX-102) Every 4 Weeks in Adult Fabry Disease Patients
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Open Label Extension of 2 mg/kg Pegunigalsidase Alfa (PRX-102) Every 4 Weeks in Adult Fabry Disease Patients
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Gastroenterology, Pharmacology / Toxicology Clinical Trial
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Gastroenterology, Pharmacology / Toxicology Clinical Trial
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Gaucher Disease Clinical Trial
A Long-term Follow-up Study of Gaucher Disease
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Cardiology / Vascular Diseases, Pharmacology / Toxicology Clinical Trial
Study of ISIS 678354 (AKCEA-APOCIII-LRx) in Patients With Hypertriglyceridemia and Established Cardiovascular Disease (CVD)
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Neurology, Pharmacology / Toxicology, Psychiatry / Psychology, Reproductive Clinical Trial
Screening for Metabolic Problems in Mothers of Children With Autism and Typically Developing Children
Status: Upcoming
Updated: 2/3/2016
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Fabry Disease Clinical Trial
Evaluation of Phenotypic Variability in Fabry Disease
Status: Upcoming,
Phase
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Pre-Clinical White Matter Changes and Associated Connectivity Effects in Fabry Disease
Status: Upcoming
Updated: 12/31/1969
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Pharmacology / Toxicology Clinical Trial
Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and II
Status: Upcoming,
Phase
I, II
Updated: 5/15/2017
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis I (MPS I) Clinical Trial
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis I (MPS I) Clinical Trial
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis I (MPS I) Clinical Trial
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Click here to add this to my saved trials
Click here to add this to my saved trials
We've found
734 Metabolic
clinical trials
Gastroenterology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Fabry Disease Clinical Trial
Updated: 12/31/1969
A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
Click here to add this to my saved trials
Cardiology / Vascular Diseases, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
Study of ISIS 678354 (AKCEA-APOCIII-LRx) in Patients With Hypertriglyceridemia and Established Cardiovascular Disease (CVD)
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
Click here to add this to my saved trials
Gaucher's Disease Clinical Trial
Updated: 6/23/2005
Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease
Status: Enrolling,
Phase
II
Updated: 6/23/2005
Click here to add this to my saved trials
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Hematology, Neurology, Pharmacology / Toxicology, Rheumatology, Orthopedics / Podiatry, Other, Reproductive Clinical Trial
Updated: 6/22/2011
Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
Status: Enrolling,
Phase
I, II
Updated: 6/22/2011
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Fabry Disease Clinical Trial
Updated: 6/25/2013
Pulmonary Disease and Exercise Tolerance in Boys With Fabry Disease
Status: Enrolling
Updated: 6/25/2013
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Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
Click here to add this to my saved trials
Endocrinology, Hematology, Immunology / Infectious Diseases, Oncology, Pharmacology / Toxicology, Reproductive Clinical Trial
Updated: 12/31/1969
A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Cardiology / Vascular Diseases, Neurology, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism
Status: Enrolling,
Phase
Updated: 12/31/1969
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Cardiology / Vascular Diseases, Endocrinology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
Effects of DPP-4 Inhibition on Triglycerides
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
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Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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Endocrinology, Hematology, Pharmacology / Toxicology, Other Clinical Trial
Updated: 8/10/2015
Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children
Status: Enrolling
Updated: 8/10/2015
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Endocrinology, Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
Longitudinal Studies of Brain Structure and Function in MPS Disorders
Status: Enrolling,
Phase
Updated: 12/31/1969
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Neurology, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/1/2015
Pharmacokinetics and Clinical Response of Tolvaptan in Neurocritical Care Patients
Status: Enrolling
Updated: 12/1/2015
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Pharmacology / Toxicology, Psychiatry / Psychology Clinical Trial
Updated: 12/31/1969
Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I
Status: Enrolling
Updated: 12/31/1969
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Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Pharmacology / Toxicology, Orthopedics / Podiatry Clinical Trial
Updated: 12/31/1969
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Status: Enrolling,
Phase
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Physician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry Disease
Status: Enrolling,
Phase
Updated: 12/31/1969
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Cardiology / Vascular Diseases, Endocrinology, Neurology, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Fatty Acid Oxidation Defects and Insulin Sensitivity
Status: Enrolling
Updated: 12/31/1969
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MPS I Clinical Trial
Updated: 12/31/1969
Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-318 in Subjects With MPS I
Status: Enrolling,
Phase
I
Updated: 12/31/1969
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Ornithine Transcarbamylase (OTC) Deficiency Clinical Trial
Updated: 12/31/1969
Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset OTC Deficiency
Status: Enrolling,
Phase
I, II
Updated: 12/31/1969
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Ornithine Transcarbamylase (OTC) Deficiency Clinical Trial
Updated: 12/31/1969
Safety and Dose-Finding Study of DTX301 (scAAV8OTC) in Adults With Late-Onset OTC Deficiency
Status: Enrolling,
Phase
I, II
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Study of the Safety and Efficacy of PRX-102 Compared to Agalsidase Beta on Renal Function
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Gaucher Disease Clinical Trial
Updated: 12/31/1969
Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
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Gaucher Disease Clinical Trial
Updated: 12/31/1969
Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease
Status: Enrolling,
Phase
IV
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged 12 to
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged 12 to
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Efficacy and Safety of Lucerastat Oral Monotherapy in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Cardiology / Vascular Diseases, Endocrinology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
Habitual Diet and Avocado Trial
Status: Enrolling
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Extension Study of 1 mg/kg Pegunigalsidase Alfa in Patients With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Extension Study of 1 mg/kg Pegunigalsidase Alfa in Patients With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Open Label Extension of 2 mg/kg Pegunigalsidase Alfa (PRX-102) Every 4 Weeks in Adult Fabry Disease Patients
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Open Label Extension of 2 mg/kg Pegunigalsidase Alfa (PRX-102) Every 4 Weeks in Adult Fabry Disease Patients
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Gastroenterology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
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Gastroenterology, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
X-linked Hypophosphatemia Disease Monitoring Program
Status: Enrolling,
Phase
Updated: 12/31/1969
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Gaucher Disease Clinical Trial
Updated: 12/31/1969
A Long-term Follow-up Study of Gaucher Disease
Status: Enrolling,
Phase
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
A Study to Evaluate the Long-term Safety and Tolerability of Lucerastat in Adult Subjects With Fabry Disease
Status: Enrolling,
Phase
III
Updated: 12/31/1969
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Cardiology / Vascular Diseases, Pharmacology / Toxicology Clinical Trial
Updated: 12/31/1969
Study of ISIS 678354 (AKCEA-APOCIII-LRx) in Patients With Hypertriglyceridemia and Established Cardiovascular Disease (CVD)
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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Musculoskeletal, Pharmacology / Toxicology, Other Clinical Trial
Updated: 12/31/1969
Tolperisone in Acute Muscle Spasm of the Back
Status: Enrolling,
Phase
II
Updated: 12/31/1969
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Neurology, Pharmacology / Toxicology, Psychiatry / Psychology, Reproductive Clinical Trial
Updated: 2/3/2016
Screening for Metabolic Problems in Mothers of Children With Autism and Typically Developing Children
Status: Upcoming
Updated: 2/3/2016
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Evaluation of Phenotypic Variability in Fabry Disease
Status: Upcoming,
Phase
Updated: 12/31/1969
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Fabry Disease Clinical Trial
Updated: 12/31/1969
Pre-Clinical White Matter Changes and Associated Connectivity Effects in Fabry Disease
Status: Upcoming
Updated: 12/31/1969
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Pharmacology / Toxicology Clinical Trial
Updated: 5/15/2017
Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and II
Status: Upcoming,
Phase
I, II
Updated: 5/15/2017
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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Mucopolysaccharidosis I (MPS I) Clinical Trial
Updated: 12/31/1969
Mucopolysaccharidosis I (MPS I) Registry
Status: Enrolling,
Phase
Updated: 12/31/1969
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Click here to add this to my saved trials
Click here to add this to my saved trials