A Pilot Study to Evaluate the Hypoglossal Nerve Stimulator in Adolescents With Down Syndrome and Obstructive Sleep Apnea

Syncardia 50cc TAH-t as a Bridge to Transplant

Phase 1 Trial of Bevacizumab Treatment for Severe Retinopathy of Prematurity

Binocular Dig Rush Game Treatment for Amblyopia

BAX 855 Previously Untreated Patient (PUP)

Developmental Impact of NICU Exposures (DINE)

A Trial of Mepolizumab Adjunctive Therapy for the Prevention of Asthma Exacerbations in Urban Children

Rare Diseases Clinical Research Network: Neurophysiological Correlates

Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged 12 to

An Extension Study of AK002 in Patients With Eosinophilic Gastritis and/or Eosinophilic Gastroenteritis

Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy

Prospective Database Registry Study of Scoliosis in Children With Cerebral Palsy

Haplo T-Cell Depleted Transplantation in High-Risk Sickle Cell Disease

Evaluate The Pharmacokinetics and Safety Of Oxycodone Oral Solution In Pediatric and Adolescent Subjects

Driving Performance of Teenage Patients With mTBI: a Longitudinal Assessment

Study of N91115 in CF Patients Who Are Heterozygous for F508del-CFTR and a Gating Mutation and Being Treated With Ivacaftor

A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocorticoid Steroids

COMPASSION XT PAS - Post-approval Study of the SAPIEN XT THV in Patients With Pulmonary Valve Dysfunction

A Multi-site Comparison of Social Visual Engagement to Clinical Diagnosis for Autism Spectrum Disorder

Cockroach Immunotherapy in Children and Adolescents

Study to Assess the Efficacy and Safety of Emapalumab in Primary Haemophagocytic Lymphohistiocytosis

A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)

Total Therapy for Infants With Acute Lymphoblastic Leukemia (ALL) I

The Treatment of Progressive Early Onset Spinal Deformities: A Multi-Center Outcome Study

Adolescent Idiopathic Scoliosis Outcomes Database Registry

Inhaled Tissue Plasminogen Activator for Acute Plastic Bronchitis

Epigenetic Reprogramming in Relapse/Refractory AML

X-linked Hypophosphatemia Disease Monitoring Program

CTL019 Out of Specification MAP for ALL or DLBCL Patients

Enhanced Support for Behavioral Barriers to Learning: An Evaluation of the SCHOOL STARS Program

Innovative Approaches to Gauge Progression of Sturge-Weber Syndrome

Bohring-Opitz Syndrome and ASXL Registry

FAST Therapy Trial of Fetal Tachyarrhythmia

High Dose Flu Vaccine in Treating Children Who Have Undergone Donor Stem Cell Transplant

Phenotypic and Genetic Assessment of Tracheal and Esophageal Birth Defects in Patients

Vincristine Sulfate Liposome Injection (Marqibo®) in Combination With UK ALL R3 Induction Chemotherapy for Children, Adolescents, and Young Adults With Relapsed ALL

Use of Mometasone Eluting Stent in Choanal Atresia

Developing e-Health Systems to Improve Growth and Nutrition in CF

A Study to Investigate the Safety and Efficacy of an Anti-IFN-gamma mAb in Children With Systemic Juvenile Idiopathic Arthritis (sJIA) Developing Macrophage Activation Syndrome/ Secondary Hemophagocytic Lymphohistiocytosis (MAS/sHLH)

Registry for Asthma Characterization and Recruitment 2

CorMatrix Cor TRICUSPID ECM Valve Replacement Study

A Study of AK002 in Patients With Eosinophilic Gastritis and/or Eosinophilic Gastroenteritis

Primary Ovarian Insufficiency: Phenotype and Optimal Treatment

Topical QR-313 in Recessive Dystrophic Epidermolysis Bullosa (RDEB) Due to Mutation(s) in Exon 73 of the COL7A1gene

A Study of Intrathecal SHP611 in Participants With Late Infantile Metachromatic Leukodystrophy

Adalimumab in JIA-associated Uveitis Stopping Trial