Longitudinal Study of Urea Cycle Disorders

Evaluating the Genetic Causes and Progression of Cholestatic Liver Diseases (LOGIC)

Closure of Muscular Ventricular Septal Defects (VSDs) With the AMPLATZER Muscular VSD (MuVSD) Occluder - Post Approval Study

Combination Chemotherapy With or Without Radiation Therapy in Treating Young Patients With Favorable-Risk Hodgkin Lymphoma

Study Evaluating KTE-C19 in Pediatric and Adolescent Subjects With Relapsed/Refractory B-precursor Acute Lymphoblastic Leukemia

A Extension Study of Udenafil in Adolescents

Fibromyalgia Integrative Training for Adolescents With Juvenile Fibromyalgia

Biliary Atresia Study in Infants and Children

Study of Two Surgical Drilling Techniques to Treat Juvenile Osteochondritis Dissecans of the Knee

Adavosertib and Local Radiation Therapy in Treating Children With Newly Diagnosed Diffuse Intrinsic Pontine Gliomas

Nivolumab With or Without Ipilimumab in Treating Younger Patients With Recurrent or Refractory Solid Tumors or Sarcomas

ATrial Tachycardia PAcing Therapy in Congenital Heart

Childhood Cancer Survivor Study

Longitudinal Study of Mitochondrial Hepatopathies

Neuroblastoma Biology Study

131I-MIBG Alone VS. 131I-MIBG With Vincristine and Irinotecan VS131I-MIBG With Vorinistat

Evaluating Progression of and Diagnostic Tools for Primary Ciliary Dyskinesia in Children and Adolescents

FibroScan™ in Pediatric Cholestatic Liver Disease (FORCE)

Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency

Gene Transfer Clinical Study in X-Linked Myotubular Myopathy

iCanCope With Sickle Cell Pain

A Study of AEB1102 (Pegzilarginase) in Patients With Arginase I Deficiency

Evaluation of Fontan-Associated Liver Disease

Molecular Phenotypes for Cystic Fibrosis Lung Disease

Computer Training Program for Younger Patients With a Brain Tumor Who Underwent Radiation Therapy

Longitudinal Assessment of Transient Elastography in Cystic Fibrosis

Study of Lorlatinib (PF-06463922)

Pilot Study of Nivolumab in Pediatric Patients With Hypermutant Cancers

A Prospective Database of Infants With Cholestasis

CTLA4-Ig (Abatacept)for Prevention of Abnormal Glucose Tolerance and Diabetes in Relatives At -Risk for Type 1

Adavosertib and Irinotecan Hydrochloride in Treating Younger Patients With Relapsed or Refractory Solid Tumors

Longitudinal Studies of Brain Structure and Function in MPS Disorders

A Randomized Controlled Trial of Leg Length Discrepancy Techniques

Observational Study of Males With Creatine Transporter Deficiency

Dyslipidemia of Obesity Intervention in Teens

BGB-290 and Temozolomide in Treating Isocitrate Dehydrogenase (IDH)1/2-Mutant Grade I-IV Gliomas