The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Patients Who Have Already Been Treated With ALN-TTR02 (Patisiran)
| Status: | Enrolling by invitation |
|---|---|
| Conditions: | Neurology, Hematology |
| Therapuetic Areas: | Hematology, Neurology |
| Healthy: | No |
| Age Range: | 18 - 85 |
| Updated: | 3/14/2019 |
| Start Date: | July 2015 |
| End Date: | August 2022 |
A Multicenter, Open-Label, Extension Study to Evaluate the Long-term Safety and Efficacy of Patisiran in Patients With Familial Amyloidotic Polyneuropathy Who Have Completed a Prior Patisiran Clinical Study
The purpose of this study is to evaluate the safety and efficacy of long-term dosing with
ALN-TTR02 (patisiran) in patients with transthyretin (TTR) mediated amyloidosis (ATTR).
ALN-TTR02 (patisiran) in patients with transthyretin (TTR) mediated amyloidosis (ATTR).
Inclusion Criteria:
- Have completed a patisiran study (i.e., completed the last efficacy visit in the
parent study) and, in the opinion of the investigator, tolerated study drug
- Be willing and able to comply with the protocol-required visit schedule and visit
requirements and provide written informed consent
Exclusion Criteria:
- Any new or uncontrolled condition that could make the patient unsuitable for
participation
We found this trial at
14
sites
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