Pentoxifylline Therapy in Biliary Atresia

Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency as Open Label Extension

N-Acetylcysteine in Biliary Atresia After Kasai Portoenterostomy

Patients Treated for Chronic Granulomatous Disease (CGD) Since 1995

Biliary Atresia Study in Infants and Children

A Safety and Efficacy Study of a Range of Linaclotide Doses Administered Orally to Children Ages 7-17 Years, With Irritable Bowel Syndrome With Constipation

Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency

Long-term Safety Study of AR101 in Subjects Who Participated in a Prior AR101 Study (ARC008)

The CDR Implementation Trial

Efficacy and Safety of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett Syndrome